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Analysis of risk factors influencing outcomes after cord blood transplantation in children with juvenile myelomonocytic leukemia: a EUROCORD, EBMT, EWOG-MDS, CIBMTR study

Identifieur interne : 004841 ( Main/Exploration ); précédent : 004840; suivant : 004842

Analysis of risk factors influencing outcomes after cord blood transplantation in children with juvenile myelomonocytic leukemia: a EUROCORD, EBMT, EWOG-MDS, CIBMTR study

Auteurs : Franco Locatelli [Italie] ; Alessandro Crotta [France] ; Annalisa Ruggeri [France, Italie] ; Mary Eapen [États-Unis] ; John E. Wagner [États-Unis] ; Margaret L. Macmillan [États-Unis] ; Marco Zecca [Italie] ; Joanne Kurtzberg [États-Unis] ; Carmem Bonfim [Brésil] ; Ajay Vora [Royaume-Uni] ; Cristina Díaz De Heredia [Espagne] ; Lochie Teague [Nouvelle-Zélande] ; Jerry Stein [Israël] ; Tracey A. O Rien [Australie] ; Henrique Bittencourt [Canada] ; Adrienne Madureira [Brésil] ; Brigitte Strahm [Allemagne] ; Christina Peters [Autriche] ; Charlotte Niemeyer [Allemagne] ; Eliane Gluckman [France] ; Vanderson Rocha [France]

Source :

RBID : PMC:3836039

Abstract

Key Points

UCBT is a suitable option for children with JMML, being able to cure a relevant proportion of patients.

Because disease recurrence remains the major cause of treatment failure after UCBT, strategies aimed at reducing relapse are desirable.


Url:
DOI: 10.1182/blood-2013-03-491589
PubMed: 23926304
PubMed Central: 3836039


Affiliations:


Links toward previous steps (curation, corpus...)


Le document en format XML

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<name sortKey="Niemeyer, Charlotte" sort="Niemeyer, Charlotte" uniqKey="Niemeyer C" first="Charlotte" last="Niemeyer">Charlotte Niemeyer</name>
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<name sortKey="Rocha, Vanderson" sort="Rocha, Vanderson" uniqKey="Rocha V" first="Vanderson" last="Rocha">Vanderson Rocha</name>
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<title xml:lang="en" level="a" type="main">Analysis of risk factors influencing outcomes after cord blood transplantation in children with juvenile myelomonocytic leukemia: a EUROCORD, EBMT, EWOG-MDS, CIBMTR study</title>
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<name sortKey="Wagner, John E" sort="Wagner, John E" uniqKey="Wagner J" first="John E." last="Wagner">John E. Wagner</name>
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<name sortKey="Zecca, Marco" sort="Zecca, Marco" uniqKey="Zecca M" first="Marco" last="Zecca">Marco Zecca</name>
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<name sortKey="Kurtzberg, Joanne" sort="Kurtzberg, Joanne" uniqKey="Kurtzberg J" first="Joanne" last="Kurtzberg">Joanne Kurtzberg</name>
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<name sortKey="Diaz De Heredia, Cristina" sort="Diaz De Heredia, Cristina" uniqKey="Diaz De Heredia C" first="Cristina" last="Díaz De Heredia">Cristina Díaz De Heredia</name>
<affiliation wicri:level="3">
<nlm:aff id="aff10">Hospital Vall d’Hebron, Barcelona, Spain;</nlm:aff>
<country xml:lang="fr">Espagne</country>
<wicri:regionArea>Hospital Vall d’Hebron, Barcelona</wicri:regionArea>
<placeName>
<settlement type="city">Barcelone</settlement>
<region nuts="2" type="region">Catalogne</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Teague, Lochie" sort="Teague, Lochie" uniqKey="Teague L" first="Lochie" last="Teague">Lochie Teague</name>
<affiliation wicri:level="1">
<nlm:aff id="aff11">Starship Hospital, Auckland, New Zealand;</nlm:aff>
<country xml:lang="fr">Nouvelle-Zélande</country>
<wicri:regionArea>Starship Hospital, Auckland</wicri:regionArea>
<wicri:noRegion>Auckland</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Stein, Jerry" sort="Stein, Jerry" uniqKey="Stein J" first="Jerry" last="Stein">Jerry Stein</name>
<affiliation wicri:level="1">
<nlm:aff id="aff12">Department of Pediatric Hematology Oncology and BMT Unit, Schneider Children’s Medical Center of Israel, Petah-Tikva, Israel;</nlm:aff>
<country xml:lang="fr">Israël</country>
<wicri:regionArea>Department of Pediatric Hematology Oncology and BMT Unit, Schneider Children’s Medical Center of Israel, Petah-Tikva</wicri:regionArea>
<wicri:noRegion>Petah-Tikva</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="O Rien, Tracey A" sort="O Rien, Tracey A" uniqKey="O Rien T" first="Tracey A." last="O Rien">Tracey A. O Rien</name>
<affiliation wicri:level="3">
<nlm:aff id="aff13">Cord & Marrow Transplant Program, Centre for Children’s Cancer & Blood Disorders, Sydney Children's Hospital, Sydney, Australia;</nlm:aff>
<country xml:lang="fr">Australie</country>
<wicri:regionArea>Cord & Marrow Transplant Program, Centre for Children’s Cancer & Blood Disorders, Sydney Children's Hospital, Sydney</wicri:regionArea>
<placeName>
<settlement type="city">Sydney</settlement>
<region type="état">Nouvelle-Galles du Sud</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Bittencourt, Henrique" sort="Bittencourt, Henrique" uniqKey="Bittencourt H" first="Henrique" last="Bittencourt">Henrique Bittencourt</name>
<affiliation wicri:level="3">
<nlm:aff id="aff14">Centre Hospitalier Universitaire Sainte-Justine, Montreal, Canada;</nlm:aff>
<country xml:lang="fr">Canada</country>
<wicri:regionArea>Centre Hospitalier Universitaire Sainte-Justine, Montreal</wicri:regionArea>
<placeName>
<settlement type="city">Montréal</settlement>
<region type="state">Québec</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Madureira, Adrienne" sort="Madureira, Adrienne" uniqKey="Madureira A" first="Adrienne" last="Madureira">Adrienne Madureira</name>
<affiliation wicri:level="3">
<nlm:aff id="aff15">Instituto Nacional de Cancer, Rio de Janeiro, Brasil;</nlm:aff>
<country xml:lang="fr">Brésil</country>
<wicri:regionArea>Instituto Nacional de Cancer, Rio de Janeiro</wicri:regionArea>
<placeName>
<settlement type="city">Rio de Janeiro</settlement>
<region type="state">État de Rio de Janeiro</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Strahm, Brigitte" sort="Strahm, Brigitte" uniqKey="Strahm B" first="Brigitte" last="Strahm">Brigitte Strahm</name>
<affiliation wicri:level="3">
<nlm:aff wicri:cut="; and" id="aff16">Division of Pediatric Hematology and Oncology, University Children's Hospital Freiburg, Freiburg, Germany</nlm:aff>
<country xml:lang="fr">Allemagne</country>
<wicri:regionArea>Division of Pediatric Hematology and Oncology, University Children's Hospital Freiburg, Freiburg</wicri:regionArea>
<placeName>
<region type="land" nuts="1">Bade-Wurtemberg</region>
<region type="district" nuts="2">District de Fribourg-en-Brisgau</region>
<settlement type="city">Fribourg-en-Brisgau</settlement>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Peters, Christina" sort="Peters, Christina" uniqKey="Peters C" first="Christina" last="Peters">Christina Peters</name>
<affiliation wicri:level="3">
<nlm:aff id="aff17">Paediatric Diseases Working Party-European Group for Blood and Marrow Transplantation, St-Anna Kinderspital, Vienna, Austria</nlm:aff>
<country xml:lang="fr">Autriche</country>
<wicri:regionArea>Paediatric Diseases Working Party-European Group for Blood and Marrow Transplantation, St-Anna Kinderspital, Vienna</wicri:regionArea>
<placeName>
<settlement type="city">Vienne (Autriche)</settlement>
<region nuts="2" type="province">Vienne (Autriche)</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Niemeyer, Charlotte" sort="Niemeyer, Charlotte" uniqKey="Niemeyer C" first="Charlotte" last="Niemeyer">Charlotte Niemeyer</name>
<affiliation wicri:level="3">
<nlm:aff wicri:cut="; and" id="aff16">Division of Pediatric Hematology and Oncology, University Children's Hospital Freiburg, Freiburg, Germany</nlm:aff>
<country xml:lang="fr">Allemagne</country>
<wicri:regionArea>Division of Pediatric Hematology and Oncology, University Children's Hospital Freiburg, Freiburg</wicri:regionArea>
<placeName>
<region type="land" nuts="1">Bade-Wurtemberg</region>
<region type="district" nuts="2">District de Fribourg-en-Brisgau</region>
<settlement type="city">Fribourg-en-Brisgau</settlement>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Gluckman, Eliane" sort="Gluckman, Eliane" uniqKey="Gluckman E" first="Eliane" last="Gluckman">Eliane Gluckman</name>
<affiliation wicri:level="3">
<nlm:aff id="aff2">Eurocord, Hôpital Saint Louis Assistance Publique-Hôpitaux de Paris, University Paris VII, Paris, France;</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Eurocord, Hôpital Saint Louis Assistance Publique-Hôpitaux de Paris, University Paris VII, Paris</wicri:regionArea>
<placeName>
<region type="region">Île-de-France</region>
<region type="old region">Île-de-France</region>
<settlement type="city">Paris</settlement>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Rocha, Vanderson" sort="Rocha, Vanderson" uniqKey="Rocha V" first="Vanderson" last="Rocha">Vanderson Rocha</name>
<affiliation wicri:level="3">
<nlm:aff id="aff2">Eurocord, Hôpital Saint Louis Assistance Publique-Hôpitaux de Paris, University Paris VII, Paris, France;</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Eurocord, Hôpital Saint Louis Assistance Publique-Hôpitaux de Paris, University Paris VII, Paris</wicri:regionArea>
<placeName>
<region type="region">Île-de-France</region>
<region type="old region">Île-de-France</region>
<settlement type="city">Paris</settlement>
</placeName>
</affiliation>
</author>
</analytic>
<series>
<title level="j">Blood</title>
<idno type="ISSN">0006-4971</idno>
<idno type="eISSN">1528-0020</idno>
<imprint>
<date when="2013">2013</date>
</imprint>
</series>
</biblStruct>
</sourceDesc>
</fileDesc>
<profileDesc>
<textClass></textClass>
</profileDesc>
</teiHeader>
<front>
<div type="abstract" xml:lang="en">
<title>Key Points</title>
<p>
<list list-type="bullet">
<list-item>
<p>UCBT is a suitable option for children with JMML, being able to cure a relevant proportion of patients.</p>
</list-item>
<list-item>
<p>Because disease recurrence remains the major cause of treatment failure after UCBT, strategies aimed at reducing relapse are desirable.</p>
</list-item>
</list>
</p>
</div>
</front>
</TEI>
<affiliations>
<list>
<country>
<li>Allemagne</li>
<li>Australie</li>
<li>Autriche</li>
<li>Brésil</li>
<li>Canada</li>
<li>Espagne</li>
<li>France</li>
<li>Israël</li>
<li>Italie</li>
<li>Nouvelle-Zélande</li>
<li>Royaume-Uni</li>
<li>États-Unis</li>
</country>
<region>
<li>Bade-Wurtemberg</li>
<li>Caroline du Nord</li>
<li>Catalogne</li>
<li>District de Fribourg-en-Brisgau</li>
<li>Latium</li>
<li>Minnesota</li>
<li>Nouvelle-Galles du Sud</li>
<li>Québec</li>
<li>Vienne (Autriche)</li>
<li>Wisconsin</li>
<li>État de Rio de Janeiro</li>
<li>Île-de-France</li>
</region>
<settlement>
<li>Barcelone</li>
<li>Fribourg-en-Brisgau</li>
<li>Montréal</li>
<li>Paris</li>
<li>Rio de Janeiro</li>
<li>Rome</li>
<li>Sydney</li>
<li>Vienne (Autriche)</li>
</settlement>
</list>
<tree>
<country name="Italie">
<region name="Latium">
<name sortKey="Locatelli, Franco" sort="Locatelli, Franco" uniqKey="Locatelli F" first="Franco" last="Locatelli">Franco Locatelli</name>
</region>
<name sortKey="Ruggeri, Annalisa" sort="Ruggeri, Annalisa" uniqKey="Ruggeri A" first="Annalisa" last="Ruggeri">Annalisa Ruggeri</name>
<name sortKey="Zecca, Marco" sort="Zecca, Marco" uniqKey="Zecca M" first="Marco" last="Zecca">Marco Zecca</name>
</country>
<country name="France">
<region name="Île-de-France">
<name sortKey="Crotta, Alessandro" sort="Crotta, Alessandro" uniqKey="Crotta A" first="Alessandro" last="Crotta">Alessandro Crotta</name>
</region>
<name sortKey="Gluckman, Eliane" sort="Gluckman, Eliane" uniqKey="Gluckman E" first="Eliane" last="Gluckman">Eliane Gluckman</name>
<name sortKey="Rocha, Vanderson" sort="Rocha, Vanderson" uniqKey="Rocha V" first="Vanderson" last="Rocha">Vanderson Rocha</name>
<name sortKey="Ruggeri, Annalisa" sort="Ruggeri, Annalisa" uniqKey="Ruggeri A" first="Annalisa" last="Ruggeri">Annalisa Ruggeri</name>
</country>
<country name="États-Unis">
<region name="Wisconsin">
<name sortKey="Eapen, Mary" sort="Eapen, Mary" uniqKey="Eapen M" first="Mary" last="Eapen">Mary Eapen</name>
</region>
<name sortKey="Kurtzberg, Joanne" sort="Kurtzberg, Joanne" uniqKey="Kurtzberg J" first="Joanne" last="Kurtzberg">Joanne Kurtzberg</name>
<name sortKey="Macmillan, Margaret L" sort="Macmillan, Margaret L" uniqKey="Macmillan M" first="Margaret L." last="Macmillan">Margaret L. Macmillan</name>
<name sortKey="Wagner, John E" sort="Wagner, John E" uniqKey="Wagner J" first="John E." last="Wagner">John E. Wagner</name>
</country>
<country name="Brésil">
<noRegion>
<name sortKey="Bonfim, Carmem" sort="Bonfim, Carmem" uniqKey="Bonfim C" first="Carmem" last="Bonfim">Carmem Bonfim</name>
</noRegion>
<name sortKey="Madureira, Adrienne" sort="Madureira, Adrienne" uniqKey="Madureira A" first="Adrienne" last="Madureira">Adrienne Madureira</name>
</country>
<country name="Royaume-Uni">
<noRegion>
<name sortKey="Vora, Ajay" sort="Vora, Ajay" uniqKey="Vora A" first="Ajay" last="Vora">Ajay Vora</name>
</noRegion>
</country>
<country name="Espagne">
<region name="Catalogne">
<name sortKey="Diaz De Heredia, Cristina" sort="Diaz De Heredia, Cristina" uniqKey="Diaz De Heredia C" first="Cristina" last="Díaz De Heredia">Cristina Díaz De Heredia</name>
</region>
</country>
<country name="Nouvelle-Zélande">
<noRegion>
<name sortKey="Teague, Lochie" sort="Teague, Lochie" uniqKey="Teague L" first="Lochie" last="Teague">Lochie Teague</name>
</noRegion>
</country>
<country name="Israël">
<noRegion>
<name sortKey="Stein, Jerry" sort="Stein, Jerry" uniqKey="Stein J" first="Jerry" last="Stein">Jerry Stein</name>
</noRegion>
</country>
<country name="Australie">
<region name="Nouvelle-Galles du Sud">
<name sortKey="O Rien, Tracey A" sort="O Rien, Tracey A" uniqKey="O Rien T" first="Tracey A." last="O Rien">Tracey A. O Rien</name>
</region>
</country>
<country name="Canada">
<region name="Québec">
<name sortKey="Bittencourt, Henrique" sort="Bittencourt, Henrique" uniqKey="Bittencourt H" first="Henrique" last="Bittencourt">Henrique Bittencourt</name>
</region>
</country>
<country name="Allemagne">
<region name="Bade-Wurtemberg">
<name sortKey="Strahm, Brigitte" sort="Strahm, Brigitte" uniqKey="Strahm B" first="Brigitte" last="Strahm">Brigitte Strahm</name>
</region>
<name sortKey="Niemeyer, Charlotte" sort="Niemeyer, Charlotte" uniqKey="Niemeyer C" first="Charlotte" last="Niemeyer">Charlotte Niemeyer</name>
</country>
<country name="Autriche">
<region name="Vienne (Autriche)">
<name sortKey="Peters, Christina" sort="Peters, Christina" uniqKey="Peters C" first="Christina" last="Peters">Christina Peters</name>
</region>
</country>
</tree>
</affiliations>
</record>

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